Rare disease

Therapies for rare conditions where patient populations are small and distribution networks are specialized.

• Asfotase Alfa

  Asfotase Alfa: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Carglumic Acid

  Carglumic Acid: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Coagulation Factor Ix Complex

  Coagulation Factor Ix Complex: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Coagulation Factor Ix Plasma Derived

  Coagulation Factor Ix Plasma Derived: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Coagulation Factor Ix Recombinant

  Coagulation Factor Ix Recombinant: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Coagulation Factor Ix Recombinant Glycopegylated

  Coagulation Factor Ix Recombinant Glycopegylated: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Coagulation Factor Viia Recombinant Human

  Coagulation Factor Viia Recombinant Human: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Coagulation Factor Viii Plasma Derived

  Coagulation Factor Viii Plasma Derived: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Coagulation Factor Viii Recombinant

  Coagulation Factor Viii Recombinant: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Coagulation Factor X Human

  Coagulation Factor X Human: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Deferasirox

  Deferasirox: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Deferiprone

  Deferiprone: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Eculizumab

  Eculizumab: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Elosulfase Alfa

  Elosulfase Alfa: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Emicizumab

  Emicizumab: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Givosiran Sodium

  Givosiran Sodium: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Hyaluronidase Nvhy Nivolumab

  Hyaluronidase Nvhy Nivolumab: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Hyaluronidase Zzxf Pertuzumab Trastuzumab

  Hyaluronidase Zzxf Pertuzumab Trastuzumab: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Lumasiran

  Lumasiran: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Miglustat

  Miglustat: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Nitisinone

  Nitisinone: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Patisiran

  Patisiran: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Pegvaliase Pqpz

  Pegvaliase Pqpz: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Ravulizumab

  Ravulizumab: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Sacrosidase

  Sacrosidase: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Sapropterin Dihydrochloride

  Sapropterin Dihydrochloride: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Sebelipase Alfa

  Sebelipase Alfa: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Taliglucerase Alfa

  Taliglucerase Alfa: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Vestronidase Alfa

  Vestronidase Alfa: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.
• Vutrisiran

  Vutrisiran: structured procurement-oriented summary for hospital, clinic, and pharmacy sourcing teams. Not medical advice; availability depends on region and authorization.